genetic mutation. – media

Could a Third Person Be Cured of HIV?

A U.K. man may be cured of HIV comes the announcement that a man in Germany may also be HIV-free thanks to a similar treatment
- Source: https://www.livescience.com/64938-hiv-cure-third-patient.html
- 645
- March 29, 2019
bone marrow genetic mutation. HIV
FDA rolls out an early and historic OK for Spark’s pioneering gene therapy

Spark Therapeutics $ONCE has scored an historic FDA approval of Luxturna, the world’s first such AAV-delivered gene therapy designed to cure a rare eye disease triggered by a genetic mutation. The drug is OK’d for RPE65 mutation linked retinal dystrophy. The treatment uses a viral vector to insert the correct copy of a gene retinal cells need to create a protein that turns light into electric signals which can restore vision lost to the disease. As with the earlier pioneering approval of the world’s first CAR-T, FDA commissioner Scott Gottlieb did the honors in recognizing the importance of this approval. And he says the agency will make sure that the regulatory path is straight and clear for the rest of the field looking to following Spark’s footsteps. “We’re at a turning point when it comes to this novel form of therapy and at the FDA, we’re focused on establishing ...
- Source: drugdu
- 760
- December 20, 2017
FDA genetic mutation. Luxturna New Approvals rare eye disease

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