Scientists at the University of Texas in Austin have found a solution to tackle the off-centered effects of the gene editing system CRISPR-Cas9, a potential treatment for diseases caused by genetic aberrations. They suggest replacing Cas9 with a different protein, Cas12a.
In what seems to be a first of its kind research, Carnegie Mellon University and Yale University researchers have successfully cured a genetic condition in a mouse model with a gene editing technique. The findings of the study showcase a potential new opportunity for further research into treating genetic disorders in utero.
A second patient has been treated in a historic gene editing study in California, and no major side effects or safety issues have emerged from the first man’s treatment nearly three months ago, doctors revealed Tuesday.
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